Sebastien Beauzile, 21, has been cured of sickle cell anemia, according to his doctors at Cohen’s Children’s Medical Center. Beauzile received a new gene therapy called Lyfgeni, created by the biotech ...
Vertex Pharmaceuticals and bluebird bio have entered into an agreement with CMS to participate in a new Medicaid payment model for gene-based sickle cell anemia treatments, the agency announced ...
SOMERVILLE, Mass.--(BUSINESS WIRE)--bluebird bio, Inc. (Nasdaq: BLUE) today announced that new and updated data from its lentiviral vector (LVV) gene addition programs in patients with sickle cell ...
Two FDA-approved gene therapies, Lyfgenia and Casgevy, will be offered through an outcomes-based Medicaid model launching in January 2025. The initiative ties payments to treatment effectiveness, ...
Stable production of anti-sickling adult hemoglobin (HBA T87Q) and elimination or significant reduction of vaso-occlusive events sustained through last follow-up for all evaluable patients (n=38), ...
Sickle cell anemia causes sickle-shaped cells to block blood flow to the lungs, leading to acute chest syndrome. Common treatment methods involve oxygen supplementation and pain management. Sickle ...
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Sickle Cell Anemia Symptoms
Sickle cell anemia refers to a group of genetic blood disorders that affect a person’s levels of hemoglobin, the protein in ...
Sickle cell anemia may qualify as a disability for people experiencing severe symptoms, allowing access to benefits. However, eligibility depends on how the condition affects daily life. Sickle cell ...
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